E ISSN: 2583-049X
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International Journal of Advanced Multidisciplinary Research and Studies

Volume 6, Issue 3, 2026

Assessment of Clinical and Functional Outcomes of SMA Under Nusinersen Using 6MWT, HFMSE, CHOP-INTEND, RULM and HINE2 can be Misleading



Author(s): Sounira Mehri, Josef Finsterer

Abstract:

None.


Keywords: Spinal Muscular Atrophy, Nusinersen, Functional Outcome, Motor Scores, Antisense Oligonucleotide

Pages: 450-451

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